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Recombinant leptin analogue

Metreleptin

Brand names: Myalepta

Adult dose

Dose: Weight-based SC OD; refer to BNF/SmPC
Route: SC
Frequency: OD

Clinical pearls

  • Generalised lipodystrophy / partial lipodystrophy with severe metabolic abnormality — specialist endocrine

Contraindications

  • General lipodystrophy with obesity
  • Hypersensitivity

Side effects

  • Hypoglycaemia
  • Lymphoma (theoretical — registry monitoring)
  • Pancreatitis
  • Anti-drug antibodies
  • Injection site reactions

Interactions

  • Insulin/sulfonylureas (hypoglycaemia — adjust)
  • Hormonal contraceptives (efficacy may decrease)

Monitoring

  • HbA1c
  • Lipids
  • Lymph nodes
  • Anti-drug antibodies

Reference: BNF; NICE HST14; SmPC; https://bnf.nice.org.uk/drugs/metreleptin/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.