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Dissociative steroid

Vamorolone

Brand names: Agamree

Adult dose

Dose: 6 mg/kg PO OD with food (max 300mg/day)
Route: PO
Frequency: OD

Clinical pearls

  • Duchenne muscular dystrophy (≥4 years) — alternative to prednisolone
  • Per NICE TA1029

Contraindications

  • Untreated systemic infection
  • Live vaccines
  • Hypersensitivity

Side effects

  • Cushingoid features (less than prednisolone)
  • HPA suppression
  • Behavioural changes
  • Vitamin D deficiency
  • Hyperglycaemia

Interactions

  • CYP3A4 modulators
  • Live vaccines

Monitoring

  • BMD
  • Growth
  • Adrenal function

Reference: BNF; NICE TA1029; SmPC; https://bnf.nice.org.uk/drugs/vamorolone/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.