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Histone deacetylase (HDAC) inhibitor

Givinostat

Brand names: Duvyzat

Adult dose

Dose: Weight-based PO BD with food — refer to BNF/SmPC
Route: PO
Frequency: BD

Clinical pearls

  • Duchenne muscular dystrophy in patients ≥6 yrs; specialist neuromuscular service

Contraindications

  • Pregnancy
  • Concurrent QT-prolonging drugs

Side effects

  • Diarrhoea
  • Thrombocytopenia
  • Hypertriglyceridaemia
  • QT prolongation

Interactions

  • QT-prolonging drugs
  • Strong CYP3A4 modulators

Monitoring

  • FBC
  • Lipids
  • ECG

Reference: BNF; SmPC; https://bnf.nice.org.uk/drugs/givinostat/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.