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Anti-FGF23 monoclonal antibody

Burosumab

Brand names: Crysvita

Adult dose

Dose: Adults: 1mg/kg SC q4w; Children: per body weight per SmPC q2w
Route: Subcutaneous
Frequency: q4w (adult) / q2w (child)

Clinical pearls

  • NICE HST8 (paediatric XLH); NICE TA791 (adult)
  • X-linked hypophosphataemia — specialist metabolic / endocrine centres
  • Royal Osteoporosis Society / BPNA guidance

Contraindications

  • Concurrent oral phosphate / vitamin D analogues
  • Severe renal impairment
  • Hyperphosphataemia
  • Hypersensitivity

Side effects

  • Injection-site reactions
  • Headache
  • Hypersensitivity
  • Restless legs
  • Hyperphosphataemia
  • Ectopic mineralisation

Interactions

  • Oral phosphate / active vitamin D analogues (avoid)

Monitoring

  • Phosphate
  • 1,25(OH)2D
  • Renal function
  • Skeletal radiology
  • Growth

Reference: BNF; NICE HST8; NICE TA791; ROS; SmPC; https://bnf.nice.org.uk/drugs/burosumab/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.