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Oral plasma kallikrein inhibitor

Berotralstat

Brand names: Orladeyo

Adult dose

Dose: 150mg PO OD
Route: Oral
Frequency: OD with food

Clinical pearls

  • NICE TA738: prophylaxis of hereditary angioedema (HAE) attacks
  • UK PIN HAE guidance; alternative to lanadelumab SC
  • Specialist immunology centre

Contraindications

  • Severe hepatic impairment
  • Concurrent strong P-gp/BCRP substrates
  • Hypersensitivity

Side effects

  • Abdominal pain
  • Diarrhoea
  • Headache
  • Reflux
  • QT prolongation
  • Hepatic enzyme elevation

Interactions

  • P-gp / BCRP substrates
  • Strong CYP3A4 inducers
  • QT-prolonging drugs

Monitoring

  • Attack frequency
  • LFTs
  • ECG (QT)
  • Adherence

Reference: BNF; NICE TA738; UK PIN HAE; SmPC; https://bnf.nice.org.uk/drugs/berotralstat/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.