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Dual IDH1/2 inhibitor

Vorasidenib (Specialist drug)

Brand names: Voranigo

Adult dose

Dose: Specialist initiation only — refer to BNF/SmPC
Route: PO
Frequency: OD

Clinical pearls

  • Grade 2 IDH-mutant astrocytoma / oligodendroglioma after surgery
  • Specialist neuro-oncology

Contraindications

  • Severe hepatic impairment
  • Pregnancy
  • Hypersensitivity

Side effects

  • Hepatotoxicity
  • Fatigue
  • Headache
  • Nausea
  • Seizures
  • QT prolongation

Interactions

  • Strong CYP3A4 modulators
  • QT-prolonging drugs

Monitoring

  • LFTs
  • ECG

Reference: BNF; SmPC; https://bnf.nice.org.uk/drugs/vorasidenib-specialist-drug/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.