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BCR-ABL tyrosine-kinase inhibitor

Ponatinib (Specialist drug)

Brand names: Iclusig

Adult dose

Dose: Specialist initiation only — refer to BNF/SmPC
Route: PO
Frequency: OD

Clinical pearls

  • CML/Ph+ ALL resistant/intolerant to other TKIs (incl. T315I mutation)
  • Specialist haem-onc — high vascular risk

Contraindications

  • Severe hepatic impairment
  • Recent arterial/venous thrombosis

Side effects

  • Arterial thrombotic events (black box)
  • Hepatotoxicity
  • HF
  • Hypertension
  • Pancreatitis
  • Severe haemorrhage

Interactions

  • Strong CYP3A4 modulators
  • Anticoagulants

Monitoring

  • BP
  • ECG
  • LFTs
  • Lipase
  • Cardiovascular assessment

Reference: BNF; NICE TA451/TA764; SmPC; https://bnf.nice.org.uk/drugs/ponatinib-specialist-drug/. Verify against your local formulary and the latest BNF before prescribing.

Related

Curated clinical cross-links plus same-class fallbacks.